Editing Hope: Gene Therapy in Duchenne Muscular Dystrophy Recorded Presentation
In this presentation, we will discuss the pathophysiology and clinical presentation of Duchenne Muscular Dystrophy, current treatment modalities, future directions of gene therapy, and barriers to care. We will describe the mechanism of action and literature supporting current treatments including glucocorticoids, exon skipping therapies, histone deacetylase inhibitors, and micro-dystrophin gene therapies.
If you attended Editing Hope: Gene Therapy in Duchenne Muscular Dystrophy on 4/14/2026, you will not be able to claim credit again for this course. However, you are welcome to still watch the content.
Target Audience
This course is intended for Advocate Health Pharmacists, Physicians, Nurses, and other interested healthcare professionals
Learning Objectives
At the completion of this activity, the participant will be able to:
- Recall pathophysiology and genetic mutations associated with Duchenne Muscular Dystrophy
- Classify medications used for Duchenne Muscular Dystrophy based on mechanism of action
- Select a treatment plan for a patient with newly diagnosed Duchenne Muscular Dystrophy
- Identify barriers to gene therapy access for patients and health systems
Faculty
- Joshua Kota, PharmD, PGY1 Pharmacy Resident - Atrium Health Wake Forest Baptist Medical Center
- Mackenzie Pearsall, PharmD, PGY1 Pharmacy Resident - Atrium Health Wake Forest Baptist Medical Center
Disclosure
The planner(s) and speaker(s) have indicated that there are no relevant financial relationships with any ineligible companies to disclose.

Accreditation Statement
In support of improving patient care, Advocate Health is jointly accredited by the Accreditation Council for Continuing Medical Education (ACCME), the Accreditation Council for Pharmacy Education (ACPE), and the American Nurses Credentialing Center (ANCC), to provide continuing education for the healthcare team.
Credit Statement(s)
American Medical Association (AMA)
Advocate Health designates this enduring activity for a maximum of 1.00 AMA PRA Category 1 Credits™. Physicians should claim only the credit commensurate with the extent of their participation in the activity.
American Nurses Credentialing Center (ANCC)
Advocate Health designates this enduring activity for a maximum of 1.00 ANCC contact hours/APRN pharmacological hours. Nurses should claim only the credit commensurate with the extent of their participation in the activity.
Accreditation Council for Pharmacy Education (ACPE)
Advocate Health designates this enduring activity for a maximum 1.00 hours of CPE credit for pharmacists. CPE credit can be claimed on the AAH CE platform within 60 days of activity completion and information will be provided to CPE Monitor. Participants should only claim credit commensurate with the extent of their participation in the activity.
Pharmacy UAN: JA0006327-0000-26-085-H01-P
Available Credit
- 1.00 AMA PRA Category 1 Credit™Aurora Health Care is accredited by the Wisconsin Medical Society to provide continuing medical education for physicians. Aurora Health Care designates this activity for a maximum of 1.00 AMA PRA Category 1 Credit(s)TM. Physicians should only claim credit commensurate with the extent of their participation in the activity.
- 1.00 AttendanceAttendance Credit
- 1.00 Approved AMA PRA Category 1 Credit™
- 1.00 Continuing Nursing Education (CE)Aurora Health Care is an approved provider of continuing nursing education by the Wisconsin Nurses Association, an accredited approver by the American Nurses Credentialing Center’s Commission on Accreditation. 1.00 contact hours have been awarded to this activity by the Wisconsin Nursing Association. To receive contact hours, participants must attend the entire activity.
- 1.00 Continuing Pharmacy Education (CPE)Aurora Health Care Department of Pharmacy Services is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education.
Price
How to Register
Click “Take Course” to complete this program.
Participation Options
This course is available to Advocate Health providers (employed and independent) and team members only.
If you attended Editing Hope: Gene Therapy in Duchenne Muscular Dystrophy on 4/14/2026, you will not be able to claim credit again for this course. However, you are welcome to still watch the content.
For Further Information
Contact the AH Continuing Pharmacy Education team at [email protected] if you have any questions or need assistance.
If you have any questions regarding registration, please contact the IPCE Office at [email protected]
Please take some time to view your profile to make sure all required fields are up to date.

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