Description: In this presentation, we will discuss the pathophysiology and clinical presentation of Duchenne Muscular Dystrophy, current treatment modalities, future directions of gene therapy, and barriers to care. We will describe the mechanism of action and literature supporting current treatments including glucocorticoids, exon skipping therapies, histone deacetylase inhibitors, and micro-dystrophin gene therapies.

Microsoft Teams Webinar link to register for the live session: Register Here

Speaker: Joshua Kota, PharmD, and Mackenzie Pearsall, PharmD, PGY1 Pharmacy Residents – Atrium Health Wake Forest Baptist Medical Center

Objectives: ​​ 

  1. Recall pathophysiology and genetic mutations associated with Duchenne Muscular Dystrophy
  2. Classify medications used for Duchenne Muscular Dystrophy based on mechanism of action
  3. Select a treatment plan for a patient with newly diagnosed Duchenne Muscular Dystrophy
  4. Identify barriers to gene therapy access for patients and health systems

Target Audience:​ Advocate Pharmacists, Physicians, Nurses, and other interested healthcare professionals

Disclosure:​ The planner(s) and speaker(s) have indicated that there are no relevant financial relationships with any ineligible companies to disclose. 

Materials: PDF icon Single Activity Flyer LIVE- Kota and Pearsall.pdfPDF icon DMD Audience Slides.pdf

Pharmacist UAN: JA0006327-0000-26-001-L01-P

Session date: 
04/14/2026 - 12:00pm to 1:00pm CDT
Location: 
Reynolds Tower-Penthouse Conference Room 1 and Virtual via Teams
United States
  • 1.00 AMA PRA Category 1 Credit™
    Aurora Health Care is accredited by the Wisconsin Medical Society to provide continuing medical education for physicians. Aurora Health Care designates this activity for a maximum of 1.00 AMA PRA Category 1 Credit(s)TM. Physicians should only claim credit commensurate with the extent of their participation in the activity.
  • 1.00 Attendance
    Attendance Credit
    • 1.00 Approved AMA PRA Category 1 Credit™
  • 1.00 Continuing Nursing Education (CE)
    Aurora Health Care is an approved provider of continuing nursing education by the Wisconsin Nurses Association, an accredited approver by the American Nurses Credentialing Center’s Commission on Accreditation. 1.00 contact hours have been awarded to this activity by the Wisconsin Nursing Association. To receive contact hours, participants must attend the entire activity.
    • 1.00 APRN Pharmacotherapeutic Contact Hours
  • 1.00 Continuing Pharmacy Education (CPE)
    Aurora Health Care Department of Pharmacy Services is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education.
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